Global Morquio Syndrome Treatment Market

Global Morquio Syndrome Treatment Market Size, Share, Growth Analysis, By Treatment(Enzyme Replacement Therapy, Other.), By Disease Type(Morquio A, Morquio B), By Distribution Channel(Hospital Pharmacies, Retail Pharmacies) - Industry Forecast 2023-2030


Report ID: SQSG35I2026 | Region: Global | Published Date: February, 2024 | Pages: 165 | Tables: 88 | Figures: 76

Global Morquio Syndrome Treatment Market Insights

Global Morquio Syndrome Treatment Market size was valued at USD 87.52 million in 2021 and is poised to grow from USD 95.72 million in 2022 to USD 188.57 million by 2030, growing at a CAGR of 9.54% in the forecast period (2023-2030).

An uncommon inherited metabolic disorder that typically affects the skeleton is referred to as Morquio syndrome, commonly known as MPS IV. Morquio syndrome is recognized as a member of the mucopolysaccharidosis group of illnesses (MPS). The body's inability to break down long sugar chains known as glycosaminoglycans is a hallmark of MPS.

One of the key factors propelling the growth of the mosquito syndrome treatment market is the rise in the number of people suffering from the condition globally. Increased government and corporate backing, as well as an increase in the demand for specific medications to treat the syndrome's sequelae, all contribute to the market's rapid expansion. The market is also impacted by the rise in mergers and partnerships between manufacturers to improve treatment alternatives. Additionally, the market for treatments for Morquio syndrome is positively impacted by the rise in healthcare spending, changes in lifestyle, technological advancements, and the occurrence of genetic illnesses. Additionally, the expansion of clinical trials creates lucrative prospects for market participants throughout the projection period of 2022 to 2028.

On the other hand, it is expected that weak reimbursement policies, particularly in the price-sensitive industry, and high production costs may restrain market expansion. The morquio syndrome treatment market is expected to have difficulties during the forecast period of 2022-2028 due to low treatment awareness.

US Morquio Syndrome Treatment Market is poised to grow at a sustainable CAGR for the next forecast year.

Market snapshot - 2023-2030

Global Market Size

USD 87.52 million

Largest Segment

Hospital Pharmacies

Fastest Growth

Hospital Pharmacies

Growth Rate

9.54% CAGR

Global Morquio Syndrome Treatment Market 2022-2028 ($ Bn)
Country Share for Asia-Pacific Region- 2021 (%)
Global Morquio Syndrome Treatment Market Size By Distribution Channel 2022-2028 ($ Bn)
Global Morquio Syndrome Treatment Market Size By Distribution Channel 2022-2028 (%)

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Global Morquio Syndrome Treatment Market Segmental Analysis

Global morquio syndrome therapy market is divided into segments based on distribution method, disease type, treatment, and Region. Based on Treatment the market is further is sub segmented into Enzyme Replacement Therapy, Based on Disease Type the market is segregated into Morquio A, Morquio B, Based on Distribution Channel the market is further sub segmented into Hospital Pharmacies, Retail Pharmacies, Online Pharmacies. Based on Region, the market is further sub segmented into Middle East and Africa, Europe, Latin America, North America, and Asia Pacific.

Morquio Syndrome Treatment Market Analysis by Distribution Channel

The chronic inflammatory demyelinating polyneuropathy market has been divided into hospitals, research & academic laboratories, and others in terms of distribution channels. Due to their extensive presence and the choice that patients have for hospitals, hospitals have accumulated the largest share of the global market. Patients are beginning to recognise the value of speciality clinics, where they can gain a deeper understanding of their ailment.

Global Morquio Syndrome Treatment Market By Distribution Channel, 2021 (%), 2021 (%)

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Global Morquio Syndrome Treatment Market Regional Insights

The Asia Pacific is also expected to dominate the market over the forecast period owing to factors such as the rising disposable income of individuals and increasing demand for passenger cars with advanced technology from the developing countries.

Due to the region's advanced technological infrastructure in the healthcare industry, North America now holds a dominant position in the morquio syndrome therapy market. Due to the region's enormous target population, Asia-Pacific is predicted to have rapid growth from 2022 to 2028.

The national part of the research also lists specific market-impacting variables and domestic market regulation changes that affect the market's present and future tendencies. Some of the key indicators utilized to anticipate the market scenario for specific countries include data points like new sales, replacement sales, national demographics, disease epidemiology, and import-export tariffs. When giving forecast analysis of the country data, it also takes into account the presence and accessibility of international brands, the difficulties they encounter owing to strong or weak competition from domestic and local brands, and the impact of sales channels.

Global Morquio Syndrome Treatment Market By Geography, 2022-2028, 2023-2030
  • Largest
  • Fastest

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Global Morquio Syndrome Treatment Market Dynamics

Morquio Syndrome Treatment Market Driver

  • It is projected that the market for treatments for Morquio syndrome would expand at a very rapid rate due to the increase in the number of products in the early and advanced stages of R&D as well as the focus on treating rare diseases. Several medications that are now in the pipelines of various firms can be predicted to undergo regulatory approvals for the marketing, if they have positive clinical trial results, as a result of the recent approval of the elosulfase alfa (VIMIZIM) drug.

Morquio Syndrome Treatment Market Restraint

  • The high cost of Morquio syndrome treatment solutions is the factor that is expected to restrain market expansion. For instance, VIMIZIM is expected to cost patients roughly US$ 380,000 annually, according to estimates. The lack of knowledge in emerging economies, as well as clinical and regulatory obstacles, are additional issues that could restrict the market's growth.

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Global Morquio Syndrome Treatment Market Competitive Landscape

In addition to recent regulatory approvals, there has been an increase in R&D for the treatment of Morquio syndrome, as shown by the increased inclusion of the condition in the clinical pipelines of the leading market participants. For the Morquio syndrome, for instance, Shire is conducting a Phase 3 Study, Ultragenyx Pharmaceutical Inc. is testing a medicine (AGT 181) in a clinical trial, and ArmaGen, Inc. is also testing a treatment for the syndrome in young patients. The market for treatments for Morquio syndrome is expanding as a result of this as well as increased disease awareness.

Morquio Syndrome Treatment Market Top Player’s Company Profiles

  • BioMarin Pharmaceutical Inc.
  • Shire (now part of Takeda Pharmaceutical Company Limited)
  • Ultragenyx Pharmaceutical Inc.
  • Abeona Therapeutics Inc.
  • RegenxBio Inc.
  • Sangamo Therapeutics Inc.
  • REGENXBIO Inc.
  • ArmaGen Inc.
  • Lysogene S.A.
  • Zymenex A/S
  • Spark Therapeutics (now part of Roche)
  • Orchard Therapeutics plc
  • Idorsia Pharmaceuticals Ltd.
  • JCR Pharmaceuticals Co., Ltd.
  • SOBI (Swedish Orphan Biovitrum AB)
  • Green Cross Corporation
  • Cabaletta Bio Inc.
  • Audentes Therapeutics (now part of Astellas Pharma Inc.)
  • Aeglea BioTherapeutics
  • Krystal Biotech Inc.

Morquio Syndrome Treatment Market Recent Development

  • In February 2021, to provide bottom hole assembly tools and services to directional drillers and operators in the Permian basin, SMG Industries, Inc., a Texas-based oilfield service firm, partnered with Christopher Equipment and Rentals, LLC, Texas.
  • In May 2021, The FDA gave Sangamo Therapeutics Inc.'s gene therapy candidate (SB-913), which is in their clinical pathway, the rare pediatric condition classification. BASF SE and NRGene (Israel) established a research agreement in October 2019, with NRGene's cloud-based artificial intelligence (AI) technology being integrated into BASF soybean research initiatives.

Global Morquio Syndrome Treatment Key Market Trends

As demonstrated by the increased inclusion of the illness in the clinical pipelines of the key market participants, there has been increased activity in R&D for the treatment of Morquio syndrome in addition to the most recent regulatory approvals. Examples include a Phase 3 Study being conducted by Ultragenyx Pharmaceutical Inc. for the Morquio syndrome, a clinical trial being conducted by the Shire for children with the syndrome, and a medication (AGT 181) being tested in clinical trials by ArmaGen, Inc. This, along with the increased public knowledge of the condition, is also fueling the market for treatments for Morquio syndrome.

Global Morquio Syndrome Treatment Market SkyQuest Analysis

SkyQuest’s ABIRAW (Advanced Business Intelligence, Research & Analysis Wing) is our Business Information Services team that Collects, Collates, Co-relates, and Analyses the Data collected using Primary Exploratory Research backed by the robust Secondary Desk research.

According to the analysis, the enzyme replacement therapy segment dominated the Global Morquio Syndrome Treatment Market in 2021 and is expected to maintain its dominance throughout the forecast period. In 2021, North America dominated the Global Morquio Syndrome Treatment Market owing to the region's highly aware and economically stable population, as well as a significantly higher number of procedures conducted.

Report Metric Details
Market size value in 2021 USD 87.52 million
Market size value in 2030 USD 188.57 million
Growth Rate 9.54%
Base year 2021
Forecast period 2023-2030
Forecast Unit (Value) USD Million
Segments covered
  • Treatment
    • Enzyme Replacement Therapy, Other.
  • Disease Type
    • Morquio A, Morquio B
  • Distribution Channel
    • Hospital Pharmacies, Retail Pharmacies, Online Pharmacies
Regions covered North America (US, Canada), Europe (Germany, France, United Kingdom, Italy, Spain, Rest of Europe), Asia Pacific (China, India, Japan, Rest of Asia-Pacific), Latin America (Brazil, Rest of Latin America), Middle East & Africa (South Africa, GCC Countries, Rest of MEA)
Companies covered
  • BioMarin Pharmaceutical Inc.
  • Shire (now part of Takeda Pharmaceutical Company Limited)
  • Ultragenyx Pharmaceutical Inc.
  • Abeona Therapeutics Inc.
  • RegenxBio Inc.
  • Sangamo Therapeutics Inc.
  • REGENXBIO Inc.
  • ArmaGen Inc.
  • Lysogene S.A.
  • Zymenex A/S
  • Spark Therapeutics (now part of Roche)
  • Orchard Therapeutics plc
  • Idorsia Pharmaceuticals Ltd.
  • JCR Pharmaceuticals Co., Ltd.
  • SOBI (Swedish Orphan Biovitrum AB)
  • Green Cross Corporation
  • Cabaletta Bio Inc.
  • Audentes Therapeutics (now part of Astellas Pharma Inc.)
  • Aeglea BioTherapeutics
  • Krystal Biotech Inc.
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Table Of Content

Executive Summary

Market overview

  • Exhibit: Executive Summary – Chart on Market Overview
  • Exhibit: Executive Summary – Data Table on Market Overview
  • Exhibit: Executive Summary – Chart on Global Morquio Syndrome Treatment Market Characteristics
  • Exhibit: Executive Summary – Chart on Market by Geography
  • Exhibit: Executive Summary – Chart on Market Segmentation
  • Exhibit: Executive Summary – Chart on Incremental Growth
  • Exhibit: Executive Summary – Data Table on Incremental Growth
  • Exhibit: Executive Summary – Chart on Vendor Market Positioning

Parent Market Analysis

Market overview

Market size

  • Market Dynamics
    • Exhibit: Impact analysis of DROC, 2021
      • Drivers
      • Opportunities
      • Restraints
      • Challenges
  • SWOT Analysis

KEY MARKET INSIGHTS

  • Technology Analysis
    • (Exhibit: Data Table: Name of technology and details)
  • Pricing Analysis
    • (Exhibit: Data Table: Name of technology and pricing details)
  • Supply Chain Analysis
    • (Exhibit: Detailed Supply Chain Presentation)
  • Value Chain Analysis
    • (Exhibit: Detailed Value Chain Presentation)
  • Ecosystem Of the Market
    • Exhibit: Parent Market Ecosystem Market Analysis
    • Exhibit: Market Characteristics of Parent Market
  • IP Analysis
    • (Exhibit: Data Table: Name of product/technology, patents filed, inventor/company name, acquiring firm)
  • Trade Analysis
    • (Exhibit: Data Table: Import and Export data details)
  • Startup Analysis
    • (Exhibit: Data Table: Emerging startups details)
  • Raw Material Analysis
    • (Exhibit: Data Table: Mapping of key raw materials)
  • Innovation Matrix
    • (Exhibit: Positioning Matrix: Mapping of new and existing technologies)
  • Pipeline product Analysis
    • (Exhibit: Data Table: Name of companies and pipeline products, regional mapping)
  • Macroeconomic Indicators

COVID IMPACT

  • Introduction
  • Impact On Economy—scenario Assessment
    • Exhibit: Data on GDP - Year-over-year growth 2016-2022 (%)
  • Revised Market Size
    • Exhibit: Data Table on Global Morquio Syndrome Treatment Market size and forecast 2021-2027 ($ million)
  • Impact Of COVID On Key Segments
    • Exhibit: Data Table on Segment Market size and forecast 2021-2027 ($ million)
  • COVID Strategies By Company
    • Exhibit: Analysis on key strategies adopted by companies

MARKET DYNAMICS & OUTLOOK

  • Market Dynamics
    • Exhibit: Impact analysis of DROC, 2021
      • Drivers
      • Opportunities
      • Restraints
      • Challenges
  • Regulatory Landscape
    • Exhibit: Data Table on regulation from different region
  • SWOT Analysis
  • Porters Analysis
    • Competitive rivalry
      • Exhibit: Competitive rivalry Impact of key factors, 2021
    • Threat of substitute products
      • Exhibit: Threat of Substitute Products Impact of key factors, 2021
    • Bargaining power of buyers
      • Exhibit: buyers bargaining power Impact of key factors, 2021
    • Threat of new entrants
      • Exhibit: Threat of new entrants Impact of key factors, 2021
    • Bargaining power of suppliers
      • Exhibit: Threat of suppliers bargaining power Impact of key factors, 2021
  • Skyquest special insights on future disruptions
    • Political Impact
    • Economic impact
    • Social Impact
    • Technical Impact
    • Environmental Impact
    • Legal Impact

Market Size by Region

  • Chart on Market share by geography 2021-2027 (%)
  • Data Table on Market share by geography 2021-2027(%)
  • North America
    • Chart on Market share by country 2021-2027 (%)
    • Data Table on Market share by country 2021-2027(%)
    • USA
      • Exhibit: Chart on Market share 2021-2027 (%)
      • Exhibit: Market size and forecast 2021-2027 ($ million)
    • Canada
      • Exhibit: Chart on Market share 2021-2027 (%)
      • Exhibit: Market size and forecast 2021-2027 ($ million)
  • Europe
    • Chart on Market share by country 2021-2027 (%)
    • Data Table on Market share by country 2021-2027(%)
    • Germany
      • Exhibit: Chart on Market share 2021-2027 (%)
      • Exhibit: Market size and forecast 2021-2027 ($ million)
    • Spain
      • Exhibit: Chart on Market share 2021-2027 (%)
      • Exhibit: Market size and forecast 2021-2027 ($ million)
    • France
      • Exhibit: Chart on Market share 2021-2027 (%)
      • Exhibit: Market size and forecast 2021-2027 ($ million)
    • UK
      • Exhibit: Chart on Market share 2021-2027 (%)
      • Exhibit: Market size and forecast 2021-2027 ($ million)
    • Rest of Europe
      • Exhibit: Chart on Market share 2021-2027 (%)
      • Exhibit: Market size and forecast 2021-2027 ($ million)
  • Asia Pacific
    • Chart on Market share by country 2021-2027 (%)
    • Data Table on Market share by country 2021-2027(%)
    • China
      • Exhibit: Chart on Market share 2021-2027 (%)
      • Exhibit: Market size and forecast 2021-2027 ($ million)
    • India
      • Exhibit: Chart on Market share 2021-2027 (%)
      • Exhibit: Market size and forecast 2021-2027 ($ million)
    • Japan
      • Exhibit: Chart on Market share 2021-2027 (%)
      • Exhibit: Market size and forecast 2021-2027 ($ million)
    • South Korea
      • Exhibit: Chart on Market share 2021-2027 (%)
      • Exhibit: Market size and forecast 2021-2027 ($ million)
    • Rest of Asia Pacific
      • Exhibit: Chart on Market share 2021-2027 (%)
      • Exhibit: Market size and forecast 2021-2027 ($ million)
  • Latin America
    • Chart on Market share by country 2021-2027 (%)
    • Data Table on Market share by country 2021-2027(%)
    • Brazil
      • Exhibit: Chart on Market share 2021-2027 (%)
      • Exhibit: Market size and forecast 2021-2027 ($ million)
    • Rest of South America
      • Exhibit: Chart on Market share 2021-2027 (%)
      • Exhibit: Market size and forecast 2021-2027 ($ million)
  • Middle East & Africa (MEA)
    • Chart on Market share by country 2021-2027 (%)
    • Data Table on Market share by country 2021-2027(%)
    • GCC Countries
      • Exhibit: Chart on Market share 2021-2027 (%)
      • Exhibit: Market size and forecast 2021-2027 ($ million)
    • South Africa
      • Exhibit: Chart on Market share 2021-2027 (%)
      • Exhibit: Market size and forecast 2021-2027 ($ million)
    • Rest of MEA
      • Exhibit: Chart on Market share 2021-2027 (%)
      • Exhibit: Market size and forecast 2021-2027 ($ million)

KEY COMPANY PROFILES

  • Competitive Landscape
    • Total number of companies covered
      • Exhibit: companies covered in the report, 2021
    • Top companies market positioning
      • Exhibit: company positioning matrix, 2021
    • Top companies market Share
      • Exhibit: Pie chart analysis on company market share, 2021(%)

Methodology

For the Global Morquio Syndrome Treatment Market, our research methodology involved a mixture of primary and secondary data sources. Key steps involved in the research process are listed below:

1. Information Procurement: This stage involved the procurement of Market data or related information via primary and secondary sources. The various secondary sources used included various company websites, annual reports, trade databases, and paid databases such as Hoover's, Bloomberg Business, Factiva, and Avention. Our team did 45 primary interactions Globally which included several stakeholders such as manufacturers, customers, key opinion leaders, etc. Overall, information procurement was one of the most extensive stages in our research process.

2. Information Analysis: This step involved triangulation of data through bottom-up and top-down approaches to estimate and validate the total size and future estimate of the Global Morquio Syndrome Treatment Market.

3. Report Formulation: The final step entailed the placement of data points in appropriate Market spaces in an attempt to deduce viable conclusions.

4. Validation & Publishing: Validation is the most important step in the process. Validation & re-validation via an intricately designed process helped us finalize data points to be used for final calculations. The final Market estimates and forecasts were then aligned and sent to our panel of industry experts for validation of data. Once the validation was done the report was sent to our Quality Assurance team to ensure adherence to style guides, consistency & design.

Analyst Support

Customization Options

With the given market data, our dedicated team of analysts can offer you the following customization options are available for the Global Morquio Syndrome Treatment Market:

Product Analysis: Product matrix, which offers a detailed comparison of the product portfolio of companies.

Regional Analysis: Further analysis of the Global Morquio Syndrome Treatment Market for additional countries.

Competitive Analysis: Detailed analysis and profiling of additional Market players & comparative analysis of competitive products.

Go to Market Strategy: Find the high-growth channels to invest your marketing efforts and increase your customer base.

Innovation Mapping: Identify racial solutions and innovation, connected to deep ecosystems of innovators, start-ups, academics, and strategic partners.

Category Intelligence: Customized intelligence that is relevant to their supply Markets will enable them to make smarter sourcing decisions and improve their category management.

Public Company Transcript Analysis: To improve the investment performance by generating new alpha and making better-informed decisions.

Social Media Listening: To analyze the conversations and trends happening not just around your brand, but around your industry as a whole, and use those insights to make better Marketing decisions.

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FAQ's

Global Morquio Syndrome Treatment Market size was valued at USD 87.52 million in 2021 and is poised to grow from USD 95.72 million in 2022 to USD 188.57 million by 2030, growing at a CAGR of 9.54% in the forecast period (2023-2030).

In addition to recent regulatory approvals, there has been an increase in R&D for the treatment of Morquio syndrome, as shown by the increased inclusion of the condition in the clinical pipelines of the leading market participants. For the Morquio syndrome, for instance, Shire is conducting a Phase 3 Study, Ultragenyx Pharmaceutical Inc. is testing a medicine (AGT 181) in a clinical trial, and ArmaGen, Inc. is also testing a treatment for the syndrome in young patients. The market for treatments for Morquio syndrome is expanding as a result of this as well as increased disease awareness. 'BioMarin Pharmaceutical Inc.', 'Shire (now part of Takeda Pharmaceutical Company Limited)', 'Ultragenyx Pharmaceutical Inc.', 'Abeona Therapeutics Inc.', 'RegenxBio Inc.', 'Sangamo Therapeutics Inc.', 'REGENXBIO Inc.', 'ArmaGen Inc.', 'Lysogene S.A.', 'Zymenex A/S', 'Spark Therapeutics (now part of Roche)', 'Orchard Therapeutics plc', 'Idorsia Pharmaceuticals Ltd.', 'JCR Pharmaceuticals Co., Ltd.', 'SOBI (Swedish Orphan Biovitrum AB)', 'Green Cross Corporation', 'Cabaletta Bio Inc.', 'Audentes Therapeutics (now part of Astellas Pharma Inc.)', 'Aeglea BioTherapeutics', 'Krystal Biotech Inc.'

It is projected that the market for treatments for Morquio syndrome would expand at a very rapid rate due to the increase in the number of products in the early and advanced stages of R&D as well as the focus on treating rare diseases. Several medications that are now in the pipelines of various firms can be predicted to undergo regulatory approvals for the marketing, if they have positive clinical trial results, as a result of the recent approval of the elosulfase alfa (VIMIZIM) drug.

The Asia Pacific is also expected to dominate the market over the forecast period owing to factors such as the rising disposable income of individuals and increasing demand for passenger cars with advanced technology from the developing countries.

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